Structure-based selectivity optimization of piperidine-pteridine derivatives as potent Leishmania pteridine reductase inhibitors

J Med Chem. 2012 Oct 11;55(19):8318-29. doi: 10.1021/jm300563f. Epub 2012 Sep 19.

Abstract

The upregulation of pteridine reductase (PTR1) is a major contributor to antifolate drug resistance in Leishmania spp., as it provides a salvage pathway that bypasses dihydrofolate reductase (DHFR) inhibition. The structure-based optimization of the PTR1 inhibitor methyl-1-[4-(2,4-diaminopteridin-6-ylmethylamino)benzoyl]piperidine-4-carboxylate (1) led to the synthesis of a focused compound library which showed significantly improved selectivity for the parasite's folate-dependent enzyme. When used in combination with pyrimethamine, a DHFR inhibitor, a synergistic effect was observed for compound 5b. This work represents a step forward in the identification of effective antileishmania agents.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Line
  • Drug Synergism
  • Fibroblasts / cytology
  • Fibroblasts / drug effects
  • Folic Acid / chemistry
  • Humans
  • Hydrophobic and Hydrophilic Interactions
  • Leishmania / drug effects
  • Leishmania / enzymology*
  • Leishmania major / drug effects
  • Leishmania major / enzymology
  • Leishmania mexicana / drug effects
  • Leishmania mexicana / enzymology
  • Molecular Docking Simulation
  • Oxidative Stress / drug effects
  • Oxidoreductases / antagonists & inhibitors*
  • Protein Binding
  • Pyrimethamine / pharmacology
  • Structure-Activity Relationship
  • Trypanocidal Agents / chemical synthesis*
  • Trypanocidal Agents / chemistry
  • Trypanocidal Agents / pharmacology

Substances

  • Trypanocidal Agents
  • Folic Acid
  • Oxidoreductases
  • pteridine reductase
  • Pyrimethamine